January 2023

Join us on Rare Disease Day February 28, 2023 and Celebrate our Research Progress

Although we are rare, we dare to do the remarkable! There are approximately 7,000 rare diseases affecting over 30 million people in the United States. Cystinosis affects approximately 2,000 people in the world, and because of CRF’s targeted strategy, our funded research has led to two FDA approvals and several clinical trials. One of the […]

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Final Report: Studies Using Zebrafish Models by Dr. Chen and Dr. Devuyst

News / Zoe Solsby

Olivier Devuyst, MD, PhD, and Zhiyong Chen, PhD, University of Zurich, Switzerland That fish in your aquarium is becoming a fighter in the battle against cystinosis! Drs. Chen and Devuyst have used zebrafish, also called “zebra danio” at your local pet store, to create a new cystinosis animal model. These fish will be used for

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Research for Ocular Cystinosis by Dr. Morgan DiLeo and Dr. Xin Fan

News / Zoe Solsby

Morgan DiLeo, PhD, and Xin Fan, PhD, University of Pittsburgh, Pennsylvania CRF continues to partner with Dr. DiLeo, whose exciting work is paving the way to a better treatment for ocular cystinosis. The study by Dr. Morgan DiLeo is focused on a sustained-release drug delivery mechanism. This mechanism has the goal of replacing the hourly

Research for Ocular Cystinosis by Dr. Morgan DiLeo and Dr. Xin Fan Read More »

Join us on Rare Disease Day February 28, 2023 and Celebrate our Research Progress

Final Report: Studies Using Zebrafish Models by Dr. Chen and Dr. Devuyst

Research for Ocular Cystinosis by Dr. Morgan DiLeo and Dr. Xin Fan

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