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Natalie Stack 5th Patient Stem Cell and Gene Therapy Trial – March 29, 2022
August 3, 2022
Tyler Joynt – 4th Patient in the Stem Cell and Gene Therapy Trial on November 15, 2021
August 3, 2022
Stem Cell Trial Phase I/II Updates by Stéphanie Cherqui, PhD
August 3, 2022

Final Report: Studies Using Zebrafish Models by Dr. Chen and Dr. Devuyst

January 24, 2023

Olivier Devuyst, MD, PhD, and Zhiyong Chen, PhD, University of Zurich, Switzerland That fish in your aquarium is becoming a fighter in the battle against

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Research for Ocular Csytinosis by Dr. Morgan DiLeo and Dr. Xin Fan

January 24, 2023

Morgan DiLeo, PhD, and Xin Fan, PhD, University of Pittsburgh, Pennsylvania CRF continues to partner with Dr. DiLeo, whose exciting work is paving the way

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Research by Dr. Jennifer Hollywood-A Drug Better than Cysteamine?

January 24, 2023

Jennifer Hollywood, PhD, University of Auckland, New Zealand Could this new drug be better than cysteamine?  Since 2020, CRF has awarded $430,422 to Dr. Jennifer

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CRF Research Helps Other Diseases and Disorders

December 6, 2022

Stéphanie Cherqui, PhD, Awarded $4.8 million CIRM Grant for Friedreich’s Ataxia   We have always known that studying a complicated disease like cystinosis would lead

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Research Progress Report by Bruno Gasnier, PhD, Paris University/CNRS)

August 3, 2022

CRF has provided over $1 million in research funding to Dr. Gasnier since 2007. In the fall of 2021, Dr. Gasnier was awarded a new

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Research Progress Report by Stéphanie Cherqui, PhD, University of California, San Diego and Corinne Antignac, MD, PhD, Imagine Institute, Paris, France

August 3, 2022

CRF awarded a research grant in 2017 to Stéphanie Cherqui, PhD, Professor, Department of Pediatrics, at the University of California, San Diego, and Corinne Antignac,

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Who We Are

  • What is Cystinosis?
  • About CRF
  • Leadership
  • Financials
  • Videos
  • Cystinosis Magazine
  • CRF News
  • Contact

For Families

  • Family Stories
  • Canadian Families
  • Current Clinical Trials
  • Cure Cystinosis International Registry (CCIR)
  • Tools for Fundraising
  • Resources

For Researchers

  • Research Overview
  • Apply for Research Grant
  • Grants Awarded
  • Published Studies
  • International Cystinosis Research Symposium

Events

  • Natalie's Wish
  • Day of Hope

Together We Shine Bright

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  • (949) 223-7610
  • info@cystinosisresearch.org
  • (949) 223-7610
  • info@cystinosisresearch.org