The First Stem Cell Transplanted Cystinosis Patient Returns Home!
We are excited to report that Jordan Janz, the first cystinosis patient to receive the autologous stem cell and gene therapy treatment as part of
CRF Awards $2,617,711 in New Grants in 2019
We are pleased to announce that CRF recently approved three new research grants totaling $856,488. The grants were awarded to Dr. Pierre Courtoy at de Duve
Thank You for Giving!
Your donations mean a brighter future for our children and adults with cystinosis. Together we are turning dreaming into doing! With the generosity and support
The First Cystinosis Patient was Transplanted!
October 7, 2019 was a day that will forever be remembered as a historic day for adults and children with cystinosis and their families. It’s
The Stem Cell and Gene Therapy Trial has Started!
We are thrilled to announce that following the FDA approval late last year, Dr. Cherqui’s clinical trial has officially begun at UCSD. CRF has funded Dr.
Rare Champions of Hope Celebration
The Cystinosis Research Foundation was recognized by Global Genes as a Rare Champion of Hope Awardee for Research and Treatment. Together, we celebrate with all
