Stem Cell and Gene Therapy Trial Update with Dr. Stéphanie Cherqui, Jordan Janz, and Barb Kulyk Presented Tuesday, October 27, 2020
We had a record of 309 people participating from 20 countries around the world. The participants represented the myriad of people in our community; adults with cystinosis, parents of children and adults with cystinosis, clinicians, researchers, and industry. Thank you Stéphanie Cherqui for the update on the trial, and to Barb Kulyk for her insights as a mom and caregiver, and an enormous thanks to Jordan for his honest and thoughtful comments about his experience as the first cystinosis patient transplanted. Thank you to everyone who participated and who asked questions. We will announce our next webinar soon! View Stem Cell Webinar Video.
Dr. Stéphanie Cherqui