Month: September 2020

Research Progress Report Update by Pierre J. Courtoy, MD, PhD

Evaluation of Ctns-/-Mice Protection by Oral Supplementation with Basic Amino-Acids:  Focus on Kidneys – Extension to Another Colony Since 2016, CRF has supported Pierre Courtoy MD, PhD, and Christophe Pierreux, PhD, with $504,728 in grant funding for their important research studies at the de Duve Institute in Brussels, Belgium. Despite the challenges with Covid-19, they …

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Stem Cell and Gene Therapy Webinar Update Video Now Available!

Stem Cell and Gene Therapy Trial Update with Dr. Stéphanie Cherqui, Jordan Janz, and Barb Kulyk Presented Tuesday, October 27, 2020 We had a record of 309 people participating from 20 countries around the world.  The participants represented the myriad of people in our community; adults with cystinosis, parents of children and adults with cystinosis, …

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