Final Report – Development and Characterization of a Rat Model of Cystinosis

In 2018, CRF awarded a grant to Olivier Devuyst, MD, PhD, University of Zurich, Switzerland, and Francesco Emma, MD, Bambino Gesù Pediatric Hospital, Rome, Italy, for their research on the Development and Characterization of a Rat Model of Cystinosis.  They successfully generated a novel Ctns-/- rat model that replicates the clinical symptoms of human nephropathic cystinosis. The rat model will be an invaluable tool for the research community. Read the report.


Olivier Devuyst, MD, PhD, Principal Investigator


Francesco Emma, MD, Co-Principal Investigator