Community Update: Novartis CYStem Phase I/II Clinical Trial in Cystinosis Posted on ClinicalTrials.gov
We are thrilled to share news about the next phase of the stem cell and gene therapy trial. This phase of the trial will bring us closer to a cure for all children and adults with cystinosis. The CYStem Phase I/II clinical trial is open to children aged 2 to 5 years with nephropathic cystinosis […]